Sparks Gene Therapy For Hemophilia B Looks To Change Up The Game
Recently, Spark Therapeutics (ONCE) reported that it had achieved positive results from its phase 1/2 study using SPK-9001 to treat patients with Hemophilia B. The most notable item from this form of treatment was able to reduce routine infusions of Factor IX concentrates.
8 Amazing CRISPR projects that could change life as we know it
Since it burst onto the scene a decade ago, CRISPR-Cas9 has shaken the field of genetics to its core. Offering a new genomic editing tool that’s faster, cheaper and more accurate than previous approaches, it opens up an astonishing breadth of possible applications.
Smart Cells releases first sample of cord blood to treat autism and parents guide to ASD
Private cord blood company, Smart Cells, has released their 20th sample of stem cells collected from cord blood and tissue to a patient to treat autism.
ALS treatment delays disease and extends life in rats
Investigators at Cedars-Sinai are exploring a new way to treat amyotrophic lateral sclerosis (ALS) by transplanting specially engineered neural cells into the brain.
The greatest gathering of national stem cell activists
The executive secretary of 3th national and international congress on the stem cell and regenerative medicine said it is essential that the Islamic Republic of Iran as the country which is moving at the borders of science and technology of the stem cells save its own excellence with holding the annual national festival in this strategic field.
Brain development influenced by the immune system
UQ Faculty of Medicines Dr. Liam Coulthard said many adult diseases originated during fetal development.
UTHealth receives funding to study stem cell therapy for traumatic injury
The University of Texas Health Science Center at Houston (UTHealth) has received funding through a public/private partnership for the first-ever clinical trial investigating a stem cell therapy for early treatment and prevention of complications after severe traumatic injury.
UCSF Welcomes First In Utero Stem Cell Transplant Baby
An in utero stem cell transplant for a critically ill second-trimester fetus has led to the birth of an apparently healthy infant. The newborn is the first patient enrolled in the world’s first clinical trial using stem cells transplanted prior to birth.
CRISPR-based Genome Editing via Non-Viral Delivery
The CRISPR-Cas9 system may be a powerful gene-editing tool, but it’s no good if the best tool in your kit can’t be applied where you want to work with it.
FDA chief Gottlieb is building a regulatory speedway to accelerate gene therapy development
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